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Found 3 Muscular Dystrophy trials

A listing of Muscular Dystrophy medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.

A Long-term Multicenter Prospective Observational Study Evaluating the Comparative Effectiveness and Safety of Sarepta Gene Transfer Therapy vs. Standard of Care in Participants with Duchenne Muscular Dystrophy under Conditions of Routine Clinical Practice

M
Marcia Felker, MD
4 years - 5 years
Male
Phase 4
Observational
What is the purpose of this study?This is a multicenter, prospective, observational Phase 4 study in the United States. The study is designed to collect both medical history and prospective data on Duchenne muscular dystrophy (DMD) treatment outcomes in participants receiving delandistrogene moxeparvovec as part of clinical care, compared to …
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Oral Ifetroban in Subjects With Duchenne Muscular Dystrophy (DMD)

J
John Parent, MD
7 years or above
Male
Phase 2
Interventional
What is the purpose of this study?Duchenne muscular dystrophy (DMD) is a devastating X-linked disease which leads to loss ofbulation between ages 7 and 13, respiratory failure and cardiomyopathy (CM) at any age, an dvitably premature death of affected young men in their late twenties. DMD is the mostgenetic disorder …
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Investigating Investigational Medication Dosing in Pediatric Duchenne Muscular Dystrophy

L
Larry Markham
8 years - 18 years
All genders
Interventional
This study investigates the use of empagliflozin in children with Duchenne muscular dystrophy, a condition that affects muscles and can lead to heart problems. The purpose of this study is to learn how the body absorbs and processes empagliflozin, which is currently used to help with heart issues in adults, …
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